2024 Rome, Italy

B-09 Kristin Karlsson
Paediatric Extrapolation - Opportunities and Challenges
Wednesday 11:30-11:50
B-10 Italo Poggesi
Extrapolating treatment to children less than 6 years old: the successful story of velmanase alfa in alpha-mannosidosis
Wednesday 11:50-12:10
B-11 Bart van Lieshout
Population pharmacokinetic analysis of guanabenz in children with Vanishing White Matter: Evaluating scaling adult drug safety and pharmacokinetics data
Wednesday 12:10-12:30